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J. Hipp, C. Bacino, L. Bird, Ina Bruenig-Traebert, D.E.C.Y. Chan, Marie-Claire de Wit, P. Fontoura, G. Hooper, Ravi Jagasia, Michelle L. Krishnan, Lorraine Murtagh, Alessandro Noci, Ana Roche Martínez, Dietmar Schwab, Mercedes Serrano, Mark D. Shen, J. Tillmann, J. Tjeertes, B. Vincenzi, E. Berry-Kravis, Azad Bonni, Muhamed Charlotte Ponghatai Mariana Katalin Stormy Susanne Barakovic Bon Boonsimma Bustamante Buzasi Chamberl, M. Barakovic, Charlotte Bon, Ponghatai Boonsimma, M. Bustamante, Katalin Buzasi, Stormy Chamberlain, Susanne Clinch, Siobhan Connor-Ahmad, Philipp Daetwyler, Oana Danila, S. Holst, Thomas Kremer, F. Lipsmeier, S. Magon, A. Messer, David Nobbs, Giuseppe Palermo, Lisa Squassante, Thomas Wiese, Jennifer M. Jamie Ralitza María Muñoz Nicola Rajsekar Shafa Bain Capal Gavrilova Cabeza Pietrafusa Rajamaran J, Jennifer M. Bain, Jamie K. Capal, R. Gavrilova, María Muñoz Cabeza, N. Pietrafusa, Rajsekar Rajamaran, Shafali S. Jeste, F. Vigevano
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The UBE3A-ATS antisense oligonucleotide rugonersen in children with Angelman syndrome: a phase 1 trial


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